CRISPR re­lieves mus­cu­lar dys­tro­phy symp­toms

The gene-edit­ing tech­nol­ogy has en­joyed suc­cess in treat­ing dogs with the con­di­tion

How It Works - - GLOBAL EYE -

CRISPR/CAS9 has been used in a study to re­lieve symp­toms of mus­cu­lar dys­tro­phy in bea­gle pup­pies. The de­bil­i­tat­ing con­di­tion causes se­vere mus­cle weak­ness and de­gen­er­a­tion and is caused by a ge­netic mu­ta­tion. CRISPR/CAS9 is a rev­o­lu­tion­ary Dna-edit­ing molec­u­lar tool that can re­pair ge­netic mu­ta­tions, and for the first time it has been suc­cess­ful in treat­ing the con­di­tion in a larger mam­mal. The re­search be­ing car­ried out at the Univer­sity of Texas is among the first to use the tech­nol­ogy in an at­tempt to cure the dis­ease. It’s hoped that the work will be a step to­wards treat­ing hu­mans with mus­cu­lar dys­tro­phy.

CRISPR/CAS9 can tar­get genes and dis­able or re­pair them or in­sert new bits of DNA

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