Therapy for blindness to cost $850,000
Afirst-of-its kind genetic treatment for blindness will cost $850,000 per patient, making it one of the most expensive medicines in the world and raising questions about the affordability of a coming wave of similar gene-targeting therapies.
The injectable treatment from Spark Therapeutics can improve the eyesight of patients with a rare genetic mutation that affects just a few thousand people in the US. Previously there has been no treatment for the condition, which eventually causes complete blindness.
Pricing questions have swirled around the treatment due to a number of unusual factors — it is intended to be a one-time treatment, it treats a very small number of patients and represents a medical breakthrough.
Previously, Spark suggested its therapy, Luxturna, could be worth more than $1 million. But the company said on Wednesday it decided on the lower price after hearing concerns from health insurers about the affordability of the treatment.
Pharmaceutical industry critics said the slightly lower cost is a distraction from the ongoing problem of unsustainable drug prices.
“The company very cleverly convinced everyone that they were going to charge a million dollars, so now they are being credited for being reasonable,” said Dr. Peter Bach, director of a policy centre at Memorial Sloan Kettering Cancer Center in New York. Approved last month, Luxturna, is the nation’s first gene therapy for an inherited disease.